1. 2018
  2. Getting Into the Rhythm With CRISPR

    VandenDriessche, T. & Chuah, M. K., 28 Sep 2018, In : Circulation Research. 123, 8, p. 928-930

    Research output: Contribution to journalEditorialResearch

  3. A calsequestrin cis-regulatory motif coupled to a cardiac troponin T promoter improves cardiac AAV9 transduction specificity

    Chamberlain, K., Riyad, J. M., Garnett, T., Kohlbrenner, E., Mookerjee, A., Elmastour, F., Benard, L., Chen, J., VandenDriessche, T., Chuah, M. K. L., Marian, A. J., Hajjar, R., Gurha, P. & Weber, T., Aug 2018, In : Human Gene Therapy. 29, 8, p. 927-937 11 p.

    Research output: Contribution to journalArticleResearchpeer-review

  4. Biopotency and Efficacy of SHP648, a Next-Generation Fix Gene Therapy Vector

    Weiller, M., Schuster, M., Coulibaly, S., Gritsch, H., Sun, K., VandenDriessche, T., Chuah, M., Rottensteiner, H. & Hoellriegl, W., May 2018, In : Molecular Therapy. 26, 5, p. 375-375

    Research output: Contribution to journalMeeting abstract (Journal)Research

  5. Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9

    Singh, K., Evens, H., Nair, N., Rincón, M. Y., Sarcar, S., Samara-Kuko, E., Chuah, M. K. & VandenDriessche, T., May 2018, In : Molecular Therapy. 26, 5, p. 1241-1254 14 p.

    Research output: Contribution to journalArticleResearchpeer-review

  6. Identification of New Muscle-Tropic Adeno-Associated Virus (AAV) Capsids for Treatment of Rare Hereditary Muscular Disorders

    El Andari, J., Tulalamba, W., Weinmann, J., VandenDriessche, T., Chuah, M. & Grimm, D., May 2018, In : Molecular Therapy. 26, 5, p. 43-44

    Research output: Contribution to journalMeeting abstract (Journal)Research

  7. Optimized liver-specific expression systems for FVIII and FIX (VUB-067-US)

    VandenDriessche, T. & Chuah, M., 15 Mar 2018, Patent No. US 2018/0071406 A1

    Research output: PatentResearch

  8. Optimized liver-specific expression systems for FVIII and FIX (VUB-067-EP)

    VandenDriessche, T. & Chuah, M., 24 Jan 2018, Patent No. EP3270944

    Research output: PatentResearch

  9. Hyperactive Factor IX Padua: A Game-Changer for Hemophilia Gene Therapy

    VandenDriessche, T. & Chuah, M. K., 3 Jan 2018, In : Molecular Therapy. 26, 1, p. 14-16 3 p.

    Research output: Contribution to journalArticleResearchpeer-review

  10. Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells

    Dastidar, S., Ardui, S., Singh, K., Majumdar, D., Shivsankaran Nair, N. N., Fu, Y., Reyon, D., Samara, E., Gerbil, M. FM., Klein, A. F., De Schrijver, W., Tipanee, J., Seneca, S., Tulalamba, W., Wang, H., Chai, Y. C., In 'T Veld, P., Furling, D., Tedesco, F. S., Vermeesch, J. R. & 3 othersJoung, J. K., Chuah, M. & VandenDriessche, T., 2018, In : Nucleic Acids Research. 46, 16, p. 8275-8298 24 p.

    Research output: Contribution to journalArticleResearchpeer-review

  11. Gene and Cell Therapy: Tearing Down Walls

    VandenDriessche, T., 2018, In : Human Gene Therapy. 29, 10, p. 1071-1073 3 p.

    Research output: Contribution to journalEditorialResearch

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