1. 2019
  2. Muscle Gene Therapy: Pluripotent Stem Cells for Gene Therapy of Hereditary Muscle Disorders

    VandenDriessche, T., Chai, Y. C., B, D. & Chuah, M., 31 Mar 2019, (Accepted/In press) Muscle Gene Therapy: Pluripotent Stem Cells for Gene Therapy of Hereditary Muscle Disorders. Duan, D. & Mendell, J. R. (eds.). Springer Nature Switzerland AG, p. 81-97 17 p.

    Research output: Chapter in Book/Report/Conference proceedingChapterResearchpeer-review

  3. Next-generation muscle-directed gene therapy by in silico vector design

    Sarcar, S., Tulalamba, W., Rincon, M. Y., Tipanee, J., Pham, H. Q., Evens, H., Boon, D., Samara-Kuko, E., Keyaerts, M., Loperfido, M., Berardi, E., Jarmin, S., In't Veld, P., Dickson, G., Lahoutte, T., Sampaolesi, M., De Bleser, P., VandenDriessche, T. & Chuah, M. K., 30 Jan 2019, In : Nature Communications. 10, 1, p. 492 18 p., 492.

    Research output: Contribution to journalArticleResearchpeer-review

  4. Distinct transduction of muscle tissue in mice after systemic delivery of AAVpo1 vectors

    Tulalamba, W., Weinmann, J., Pham, Q. H., El Andari, J., VandenDriessche, T., Chuah, M. K. & Grimm, D., 2019, In : Gene Therapy.

    Research output: Contribution to journalArticleResearchpeer-review

  5. 2018
  6. Getting Into the Rhythm With CRISPR

    VandenDriessche, T. & Chuah, M. K., 28 Sep 2018, In : Circulation Research. 123, 8, p. 928-930 3 p.

    Research output: Contribution to journalEditorialResearch

  7. Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells

    Dastidar, S., Ardui, S., Singh, K., Majumdar, D., Shivsankaran Nair, N. N., Fu, Y., Reyon, D., Samara, E., Gerbil, M. FM., Klein, A. F., De Schrijver, W., Tipanee, J., Seneca, S., Tulalamba, W., Wang, H., Chai, Y. C., In 'T Veld, P., Furling, D., Tedesco, F. S., Vermeesch, J. R. & 3 othersJoung, J. K., Chuah, M. & VandenDriessche, T., 19 Sep 2018, In : Nucleic Acids Research. 46, 16, p. 8275-8298 24 p.

    Research output: Contribution to journalArticleResearchpeer-review

  8. A Calsequestrin Cis-Regulatory Motif Coupled to a Cardiac Troponin T Promoter Improves Cardiac Adeno-Associated Virus Serotype 9 Transduction Specificity

    Chamberlain, K., Riyad, J. M., Garnett, T., Kohlbrenner, E., Mookerjee, A., Elmastour, F., Benard, L., Chen, J., VandenDriessche, T., Chuah, M. K. L., Marian, A. J., Hajjar, R., Gurha, P. & Weber, T., Aug 2018, In : Human Gene Therapy. 29, 8, p. 927-937 11 p.

    Research output: Contribution to journalArticleResearchpeer-review

  9. Efficient In Vivo Liver-Directed Gene Editing Using CRISPR/Cas9

    Singh, K., Evens, H., Nair, N., Rincón, M. Y., Sarcar, S., Samara-Kuko, E., Chuah, M. K. & VandenDriessche, T., 2 May 2018, In : Molecular Therapy. 26, 5, p. 1241-1254 14 p.

    Research output: Contribution to journalArticleResearchpeer-review

  10. Biopotency and Efficacy of SHP648, a Next-Generation Fix Gene Therapy Vector

    Weiller, M., Schuster, M., Coulibaly, S., Gritsch, H., Sun, K., VandenDriessche, T., Chuah, M., Rottensteiner, H. & Hoellriegl, W., May 2018, In : Molecular Therapy. 26, 5, p. 375-375

    Research output: Contribution to journalMeeting abstract (Journal)Research

  11. Haemophilia gene therapy: From trailblazer to gamechanger

    Evens, H., Chuah, M. K. & VandenDriessche, T., May 2018, In : Haemophilia. 24, p. 50-59 10 p.

    Research output: Contribution to journalArticleResearchpeer-review

  12. Identification of New Muscle-Tropic Adeno-Associated Virus (AAV) Capsids for Treatment of Rare Hereditary Muscular Disorders

    El Andari, J., Tulalamba, W., Weinmann, J., VandenDriessche, T., Chuah, M. & Grimm, D., May 2018, In : Molecular Therapy. 26, 5, p. 43-44

    Research output: Contribution to journalMeeting abstract (Journal)Research

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